Batten’s disease currently has no cure. However, scientific advances & promising new research give us a glimmer of hope.
This consists of therapies and experimental stage treatments which require a significant financial investment and therefore our main objective is to raise funds through our association Hodeilargi.
An experimental genetic therapy in the USA.
Science has advanced regarding the development of genetic therapies focussing on genetic disorders such as Batten’s an other similar diseases.
In the case of Batten CLN6 disease that affects both Hodei and Ilargi, there is a line of research in gene therapy with potential to slow the course of the disease, developed in the United States by Amicus Therapeutics together with the Research Institute of Nationwide Children’s Hospital.